For many East Tennessee kids, running and playing comes as naturally to them as breathing. For Jerrick Johnson and his mother ...

The mice tested in the study modeled human Hurler syndrome, a subset of disease known as mucopolysaccharidosis type I (MPS I), one of the most common types of lysosomal storage diseases. MPS I is a ...

LONDON--(BUSINESS WIRE)--Technavio has announced its pipeline analysis report on the Hurler syndrome market. The report includes a detailed analysis of the pipeline molecules under investigation ...

Gene therapy being developed as a one-time treatment to address the underlying cause of the disease by inserting a functional copy of the human IDUA gene into a patient’s own hematopoietic stem cells ...

We were unable to process your request. Please try again later. If you continue to have this issue please contact customerservice@slackinc.com. Back to Healio The FDA has issued rare pediatric disease ...

Dublin, July 22, 2025 (GLOBE NEWSWIRE) -- The "Mucopolysaccharidosis I (MPS I) (Hurler Syndrome ) - Global Clinical Trials Review, 2025" clinical trials has been added to ResearchAndMarkets.com's ...

Gene therapy might soon offer a new option for children with a rare genetic disorder that damages tissues throughout the body, researchers are reporting. In a study of eight children with the ...

Research using special adult stem cells is promising new hope for better treatments for the devastating genetic disease Hurler’s syndrome. University of Adelaide research using special adult stem ...

A deficiency of β-galactosidase (pH 5.0) was found in frozen tissues (brain, liver, kidney and spleen) from 10 patients with Hurler's syndrome (Types 1–3). The diminished activity of this enzyme was ...

Ezra Rupple concentrated as his left hand guided a pencil over the piece of paper. His grip was firm as he neatly formed the words: "The quick brown fox jumps over the lazy dog." "I practiced about 15 ...

DUBLIN--(BUSINESS WIRE)--The "US Hurler's Syndrome Market and Competitive Landscape - 2019" report has been added to ResearchAndMarkets.com's offering. This latest research provides comprehensive ...

Researchers used blood platelets and bone marrow cells to deliver potentially curative gene therapy to mouse models of the human genetic disorder Hurler syndrome -- an often fatal condition that ...