Scientists have developed a novel approach of genome editing to repair muscle stem (satellite) cells, offering new hope for ...
The powerful gene editing technology CRISPR is one small step closer to treating a human disease. In a new paper published in Science, researchers led by Eric Olson, professor and chair of molecular ...
Muscular Dystrophies are a group of genetic conditions characterized by muscle weaknesses. They are genetic conditions and have different sub-categories depending on which area of muscle mass is ...
A Community Event for Duchenne Muscular Dystrophy Awareness Brick, United States – January 1, 2026 / Steps for Hope 5K / The ...
HHS has announced the addition of Duchenne muscular dystrophy and metachromatic leukodystrophy to the Recommended Uniform ...
Muscular Dystrophy (MD) is more than a medical condition—it's a journey that reshapes lives. Imagine trying to climb stairs, run, or even stand, only to find your muscles not cooperating. That’s the ...
ST. LOUIS — When families streamed into Forest Park Sunday morning, many of them were there for a walk to cover new ground in the fight against muscular dystrophy. "You know for me the diagnosis was ...
Duchenne muscular dystrophy has several approved drugs, including a gene therapy that provides children who have the rare, inherited muscle-wasting disease the option of a one-time treatment. But each ...
The Food and Drug Administration (FDA) has approved the first gene therapy for the treatment of Duchenne muscular dystrophy (DMD) in children from age 4 through 5 years of age. Pediatric patients who ...
The MDA's 75th anniversary conference highlights advancements in gene therapy, precision medicine, and patient-centered care for muscular dystrophy. Discussions focus on equitable access to ...
Multiplatinum songwriter, Worcester native and Doherty High School graduate Donnie Demers died unexpectedly Dec. 22. He was ...