Fox News

Muscular dystrophy breakthrough: FDA approves first-ever gene therapy for rare children’s disease

The Food and Drug Administration (FDA) has approved the first gene therapy for the treatment of Duchenne muscular dystrophy (DMD) in children from age 4 through 5 years of age. Pediatric patients who ...
WVXU

Muscular dystrophy may be able to be prevented, Cincinnati Children's researchers say

Muscle tissue damage appears when muscular dystrophy is induced in a mouse model (middle). But when researchers block the function of two genes that drive unwanted mitochondrial pore formation (right) ...
KSBW The Central Coast

First gene therapy for deadly form of muscular dystrophy gets FDA approval for young kids

The first gene therapy for a deadly form of muscular dystrophy received preliminary U.S. approval on Thursday despite concerns from some government scientists about the treatment's ability to help ...
Morningstar

Parent Project Muscular Dystrophy Announces Children's Hospital of Philadelphia as Certified Duchenne Care Center, Recipient of Inaugural Clinical Research Designation

WASHINGTON, June 12, 2025 /PRNewswire/ -- Parent Project Muscular Dystrophy (PPMD), a nonprofit organization leading the fight to end Duchenne muscular dystrophy (Duchenne), is pleased to announce the ...

New Hanover County firefighters collecting donations for muscular dystrophy

WILMINGTON, N.C. (WECT) -New Hanover County Fire Rescue firefighters are collecting donations at intersections around ...